RNARISE™: A Compact, Non-Viral Self-Amplifying RNA Platform for Therapeutics
- Leverage AI-driven discovery to identify novel eukaryotic RNA replicases and engineer a 1.8 kb non-viral self-amplifying system
- Demonstrate biochemical validation and cell data confirming functional RNA amplification
- Translate platform innovation toward therapeutic application through early protein replacement programs in MPSIIIA/B